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Browsing by Author Giraldo, Pilar

Showing results 1 to 15 of 15
Issue DateTitleAuthor(s)TypeМp-cat.
2016Enzyme replacement therapy with taliglucerase alfa: 36‐month safety and efficacy results in adult patients with Gaucher disease previously treated with imiglucerasePastores, Gregory M.; Shankar, Suma P.; Petakov, Milan ; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J.; Szer, Jeffrey; Chertkoff, Raul; Brill‐Almon, Einat; Zimran, AriArticle
21M21
2016Long-term efficacy and safety results of taliglucerase alfa through 5 years in adult treatment-naive patients with Gaucher diseaseChertkoff, Raul; Zimran, Ari; Duran, Gloria; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Petakov, Milan S; Eduardo, Solorio-Meza Sergio; Cooper, Peter A; Varughese, Sheeba;
Alon, Sari; Brill-Almon, Einat;
Conference Paper
Mp. category will be shown later
2019Long-term efficacy and safety results of taliglucerase alfa through 5 years in adult treatment-naïve patients with Gaucher diseaseZimran, Ari; Durán, Gloria; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Petakov, Milan ; Terreros, Muñoz Eduardo; Solorio-Meza, Sergio Eduardo; Cooper, Peter A.; Varughese, Sheeba;
Alon, Sari; Chertkoff, Raul;
Article
22M22
2013Long-term safety and efficacy data of taliglucerase alfa, a Plant cell-expressed recombinant glucocerebrosidase, in the treatment of naive Gaucher disease patients: 36-Month ResultsZimran, Ari; Mehta, Atul; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Amato, Dominick J; Petakov, Milan S; Terreros, Munoz Eduardo; Eduardo, Solorio-Meza Sergio; Duran, Gloria;
Elstein, Deborah; Chertkoff, Raul; Brill-Almon, Einat;
Conference Paper
Mp. category will be shown later
2018Long-term safety and efficacy of taliglucerase alfa in pediatric Gaucher disease patients who were treatment-naïve or previously treated with imigluceraseZimran, Ari; Gonzalez-Rodriguez, Derlis Emilio; Abrahamov, Aya; Cooper, Peter A.; Varughese, Sheeba; Giraldo, Pilar; Petakov, Milan ; Tan, Ee Shien; Chertkoff, RaulArticle
22M22
2016Long‐term efficacy and safety results of taliglucerase alfa up to 36 months in adult treatment‐naïve patients with Gaucher diseaseZimran, Ari; Durán, Gloria; Mehta, Atul; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Amato, Dominick J.; Petakov, Milan ; Muñoz, Eduardo Terreros; Solorio‐Meza, Sergio Eduardo;
Cooper, Peter A.; Varughese, Sheeba; Chertkoff, Raul; Brill‐Almon, Einat;
Article
21M21
2010Peripheral neuropathy in adult type 1 Gaucher disease: a 2-year prospective observational studyBiegstraaten, Marieke; Mengel, Eugen; Maródi, Laszlo; Petakov, Milan ; Niederau, Claus; Giraldo, Pilar; Hughes, Derralyn; Mrsic, Mirando; Mehta, Atul; Hollak, Carla E. M.;
van, Schaik Ivo N.;
Article
21a+M21a+
2012Pivotal trial with plant cell-expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher disease (Erratum - errors in Affiliations - vol 118, pg 5767, 2011)</strong></font>Zimran, Ari; Brill-Almon, Einat; Chertkoff, Raul; Petakov, Milan S; Blanco-Favela, Francisco; Munoz, Eduardo Terreros; Solorio, Meza Sergio Eduardo; Amato, Dominick J; Duran, Gloria; Giona, Florina;
Heitner, Rene; Rosenbaum, Hanna; Giraldo, Pilar; Mehta, Atul; Park, Glen; Phillips, Mici; Elstein, Deborah; Altarescu, Gheona; Szleifer, Mali; Hashmueli, Sharon; Aviezer, David;
Other
Mp. category will be shown later
2011Pivotal trial with plant cell–expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher diseaseZimran, Ari; Brill-Almon, Einat; Chertkoff, Raul; Petakov, Milan ; Blanco-Favela, Francisco; Muñoz, Eduardo Terreros; Solorio-Meza, Sergio E.; Amato, Dominick; Duran, Gloria; Giona, Fiorina;
Heitner, Rene; Rosenbaum, Hanna; Giraldo, Pilar; Mehta, Atul; Park, Glen; Phillips, Mici; Elstein, Deborah; Altarescu, Gheona; Szleifer, Mali; Hashmueli, Sharon; Aviezer, David;
Article
21a+M21a+
2011Plant Cell Expressed Recombinant Glucocerebrosidase - taliglucerase alfa - as Therapy for Gaucher Disease in Patients Previously Treated with imiglucerasePastores, Gregory M; Fernhoff, Paul M; Szer, Jeffrey; Petakov, Milan S; Cox, Timothy M; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J; Mengel, Eugen; Chertkoff, Raul;
Almon-Brill, Einat; Zimran, Ari;
Conference Paper
Mp. category will be shown later
2012Plant Cell Expressed Recombinant Glucocerebrosidase - Taliglucerase alfa as Therapy for Gaucher Disease in Patients Previously Treated with ImiglucerasePastores, Gregory M; Fernhoff, Paul M; Szer, Jeffrey; Petakov, Milan S; Cox, Timothy M; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J; Mengel, Eugen; Chertkoff, Raul;
Almon-Brill, Einat; Zimran, Ari;
Conference Paper
Mp. category will be shown later
2013Plant cell-expressed recombinant glucocerebrosidase: Taliglucerase alfa as therapy for Gaucher disease in adults patients previously treated with imiglucerase: 24-month resultsPastores, Gregory M; Shankar, Suma P; Szer, Jeffrey; Petakov, Milan S; Cox, Timothy M; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J; Mengel, Eugen; Chertkoff, Raul;
Almon-Brill, Einat; Zimran, Ari;
Conference Paper
Mp. category will be shown later
2010Polyneuropathy in Type 1 Gaucher disease: A two-year, multinational, prospective observational studyBiegstraaten, Marieke; Mengel, Eugen; Marodi, Laszlo; Petakov, Milan S; Niederau, Claus; Giraldo, Pilar; Hughes, Derralyn; Mrsic, Mirando; Mehta, Atul; Hollak, Carla EM;
van, Schaik Ivo N;
Conference Paper
Mp. category will be shown later
2007Prevalence of polyneuropathy in adult type 1 Gaucher disease (GD1) - a multinational prospective observational studyHollak, Carla E. M.; Biegstraaten, Marieke; van Schaik, Ivo N.; Mengel, Eugen; Marodi, Laszlo; Petakov, Milan S. ; Niederau, Claus; Giraldo, Pilar; Hughes, Derralyn; Mršić, Mirando;
Mehta, Atul;
Conference Paper
Mp. category will be shown later
2012The cognitive profile of type 1 Gaucher disease patientsBiegstraaten, Marieke; Wesnes, Keith A.; Luzy, Cécile; Petakov, Milan ; Mrsic, Mirando; Niederau, Claus; Giraldo, Pilar; Hughes, Derralynn; Mehta, Atul; Mengel, Karl-Eugen;
Hollak, Carla E. M; Maródi, László; van, Schaik Ivo N.;
Article
21M21