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Browsing by Author Assouline, Sarit
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Issue Date | Title | Author(s) | Type | М-cat. |
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2015 | Effect of Oral Eliglustat on Splenomegaly in Patients With Gaucher Disease Type 1 | Mistry, Pramod K.; Lukina, Elena; Ben, Turkia Hadhami; Amato, Dominick; Baris, Hagit; Dasouki, Majed; Ghosn, Marwan; Mehta, Atul; Packman, Seymour; Pastores, Gregory; | Article | 21aM21a |
2017 | Outcomes after 18 months of eliglustat therapy in treatment-naïve adults with Gaucher disease type 1: The phase 3 ENGAGE trial | Mistry, Pramod K.; Lukina, Elena; Ben, Turkia Hadhami; Shankar, Suma P.; Baris, Hagit; Ghosn, Marwan; Mehta, Atul; Packman, Seymour; Pastores, Gregory; Petakov, Milan ;
Assouline, Sarit; Balwani, Manisha; Danda, Sumita; Hadjiev, Evgueniy; Ortega, Andres; Gaemers, Sebastiaan J. M.; Tayag, Regina; Peterschmitt, M. Judith;
| Article | 21M21 |