Browsing eNauka

Browsing by Project Avexis/

Showing results 1 to 2 of 2
Issue DateTitleAuthor(s)TypeМp-cat.
2022Clinical Trial Readiness for Spinal Muscular Atrophy: Experience of an International Educational-Training InitiativeTizzano, Eduardo F; Christie-Brown, Vanessa; Baranello, Giovanni; Germanenko, Olga; Gray, Allyson; Krstic, Marija; Lilien, Charlotte; Patel, Hinal; Servais, Laurent; Scoto, MariacristinaArticle
21M21
2022The SOD1-mediated ALS phenotype shows a decoupling between age of symptom onset and disease durationOpie-Martin, Sarah; ...; Stevic, Zorica D; ...; (broj, koautora 49)Article
21a+M21a+