eNauka - pregled
Pregled prema Autor Mistry, Pramod K
Prikaz rezultata 1 do 4 od 4
Godina | Naslov | Autor(i) | Tip rezultata | Mp-kat. |
---|---|---|---|---|
2013 | A phase 3, randomized, double-blind, placebo-controlled, multi-center study to investigate the efficacy and safety of eliglustat in patients with Gaucher disease type 1 (ENGAGE): Results after 9 months of treatment | Mistry, Pramod K; Lukina, Elena; Ben, Dridi Marie-Francoise; Amato, Dominick J; Baris, Hagit; Dasouki, Majed; Ghosn, Marwan; Mehta, Atul; Packman, Seymour; Pastores, Gregory M;
Petakov, Milan S; Peterschmitt, Judith M;
| Konferencijski rad | Mp kategorija će biti prikazana naknadno. |
2021 | Clinical outcomes after 4.5 years of eliglustat therapy for Gaucher disease type 1: Phase 3 ENGAGE trial final results | Mistry, Pramod K; ...; Petakov, Milan S; ...; (broj, koautora 18) | Naučni članak | 21aM21a - Rad u međ. časopisu izuzetnih vrednosti |
2020 | Individual patient responses to eliglustat in treatment-naive adults with Gaucher disease type 1: Final data from the phase 3 ENGAGE trial | Mistry, Pramod K; ...; Petakov, Milan S; ...; (broj, koautora 18) | Konferencijski rad | Mp kategorija će biti prikazana naknadno. |
2017 | Long-term results of ENGAGE: a phase 3, randomized, double blind, placebo-controlled, multi center study investigating the efficacy and safety of eliglustat in adults with type 1 Gaucher disease | Mistry, Pramod K; ...; Petakov, Milan S; ...; (broj, koautora 18) | Konferencijski rad | Mp kategorija će biti prikazana naknadno. |