eNauka - pregled
Pregled prema Autor Rosenbaum, Hanna
Prikaz rezultata 1 do 14 od 14
Godina | Naslov | Autor(i) | Tip rezultata | Mp-kat. |
---|---|---|---|---|
2019 | Addendum to Letter to the Editor: Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1 (✓) | Mistry, Pramod K.; Balwani, Manisha; Baris, Hagit N.; Turkia, Hadhami Ben; Burrow, T. Andrew; Charrow, Joel; Cox, Gerald F.; Danda, Sumita; Dragosky, Marta; Drelichman, Guillermo;
El-Beshlawy, Amal; Fraga, Cristina; Freisens, Selena; Gaemers, Sebastiaan; Hadjiev, Evgueniy; Kishnani, Priya S.; Lukina, Elena; Maison-Blanche, Pierre; Martins, Ana Maria; Pastores, Gregory; Petakov, Milan ; Peterschmitt, M. Judith; Rosenbaum, Hanna; Rosenbloom, Barry; Underhill, Lisa H.; Cox, Timothy M.;
| Naučni članak | 22M22 - Rad u istaknutom međ. časopisu |
2016 | Enzyme replacement therapy with taliglucerase alfa: 36‐month safety and efficacy results in adult patients with Gaucher disease previously treated with imiglucerase | Pastores, Gregory M.; Shankar, Suma P.; Petakov, Milan ; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J.; Szer, Jeffrey; Chertkoff, Raul; Brill‐Almon, Einat; Zimran, Ari | Naučni članak | 21M21 - Rad u vrhunskom međ. časopisu |
2012 | Long Term Bone Marrow Responses, as Measured by Quantitative Chemical Shift Imaging (QCSI) MRI, Following Treatment With Taliglucerase Alfa in Patients with Type 1 Gaucher Disease | van, Dussen Laura; Hollak, Carla EM; Zimran, Ari; Petakov, Milan S; Rosenbaum, Hanna; Aviezer, David; Brill-Almon, Einat; Chertkoff, Raul; Maas, Mario | Konferencijski rad | Mp kategorija će biti prikazana naknadno. |
2012 | Long Term Safety and Efficacy Data of Taliglucerase Alfa, a Plant Cell Expressed Recombinant Glucocerebrosidase, in Treatment Of Naive Gaucher Disease Patients | Zimran, Ari; Heitner, Rene; Mehta, Atul; Giraldo, Pllar; Rosenbaum, Hanna; Giona, Florina; Amato, Dominick J; Petakov, Milan S; Meillon, Garcia Luis Antonio; Solorio, Meza Sergio Eduardo;
Duran, Gloria; Elstein, Deborah; Brill-Almon, Einat;
| Konferencijski rad | Mp kategorija će biti prikazana naknadno. |
2016 | Long-term efficacy and safety results of taliglucerase alfa through 5 years in adult treatment-naive patients with Gaucher disease | Chertkoff, Raul; Zimran, Ari; Duran, Gloria; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Petakov, Milan S; Eduardo, Solorio-Meza Sergio; Cooper, Peter A; Varughese, Sheeba;
Alon, Sari; Brill-Almon, Einat;
| Konferencijski rad | Mp kategorija će biti prikazana naknadno. |
2019 | Long-term efficacy and safety results of taliglucerase alfa through 5 years in adult treatment-naïve patients with Gaucher disease (✓) | Zimran, Ari; Durán, Gloria; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Petakov, Milan ; Terreros, Muñoz Eduardo; Solorio-Meza, Sergio Eduardo; Cooper, Peter A.; Varughese, Sheeba;
Alon, Sari; Chertkoff, Raul;
| Naučni članak | 22M22 - Rad u istaknutom međ. časopisu |
2013 | Long-term safety and efficacy data of taliglucerase alfa, a Plant cell-expressed recombinant glucocerebrosidase, in the treatment of naive Gaucher disease patients: 36-Month Results | Zimran, Ari; Mehta, Atul; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Amato, Dominick J; Petakov, Milan S; Terreros, Munoz Eduardo; Eduardo, Solorio-Meza Sergio; Duran, Gloria;
Elstein, Deborah; Chertkoff, Raul; Brill-Almon, Einat;
| Konferencijski rad | Mp kategorija će biti prikazana naknadno. |
2016 | Long‐term efficacy and safety results of taliglucerase alfa up to 36 months in adult treatment‐naïve patients with Gaucher disease | Zimran, Ari; Durán, Gloria; Mehta, Atul; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Amato, Dominick J.; Petakov, Milan ; Muñoz, Eduardo Terreros; Solorio‐Meza, Sergio Eduardo;
Cooper, Peter A.; Varughese, Sheeba; Chertkoff, Raul; Brill‐Almon, Einat;
| Naučni članak | 21M21 - Rad u vrhunskom međ. časopisu |
2012 | Pivotal trial with plant cell-expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher disease (Erratum - errors in Affiliations - vol 118, pg 5767, 2011)</strong></font> | Zimran, Ari; Brill-Almon, Einat; Chertkoff, Raul; Petakov, Milan S; Blanco-Favela, Francisco; Munoz, Eduardo Terreros; Solorio, Meza Sergio Eduardo; Amato, Dominick J; Duran, Gloria; Giona, Florina;
Heitner, Rene; Rosenbaum, Hanna; Giraldo, Pilar; Mehta, Atul; Park, Glen; Phillips, Mici; Elstein, Deborah; Altarescu, Gheona; Szleifer, Mali; Hashmueli, Sharon; Aviezer, David;
| Ostalo | Mp kategorija će biti prikazana naknadno. |
2011 | Pivotal trial with plant cell–expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher disease | Zimran, Ari; Brill-Almon, Einat; Chertkoff, Raul; Petakov, Milan ; Blanco-Favela, Francisco; Muñoz, Eduardo Terreros; Solorio-Meza, Sergio E.; Amato, Dominick; Duran, Gloria; Giona, Fiorina;
Heitner, Rene; Rosenbaum, Hanna; Giraldo, Pilar; Mehta, Atul; Park, Glen; Phillips, Mici; Elstein, Deborah; Altarescu, Gheona; Szleifer, Mali; Hashmueli, Sharon; Aviezer, David;
| Naučni članak | 21aM21a - Rad u međ. časopisu izuzetnih vrednosti |
2011 | Plant Cell Expressed Recombinant Glucocerebrosidase - taliglucerase alfa - as Therapy for Gaucher Disease in Patients Previously Treated with imiglucerase | Pastores, Gregory M; Fernhoff, Paul M; Szer, Jeffrey; Petakov, Milan S; Cox, Timothy M; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J; Mengel, Eugen; Chertkoff, Raul;
Almon-Brill, Einat; Zimran, Ari;
| Konferencijski rad | Mp kategorija će biti prikazana naknadno. |
2012 | Plant Cell Expressed Recombinant Glucocerebrosidase - Taliglucerase alfa as Therapy for Gaucher Disease in Patients Previously Treated with Imiglucerase | Pastores, Gregory M; Fernhoff, Paul M; Szer, Jeffrey; Petakov, Milan S; Cox, Timothy M; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J; Mengel, Eugen; Chertkoff, Raul;
Almon-Brill, Einat; Zimran, Ari;
| Konferencijski rad | Mp kategorija će biti prikazana naknadno. |
2013 | Plant cell-expressed recombinant glucocerebrosidase: Taliglucerase alfa as therapy for Gaucher disease in adults patients previously treated with imiglucerase: 24-month results | Pastores, Gregory M; Shankar, Suma P; Szer, Jeffrey; Petakov, Milan S; Cox, Timothy M; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J; Mengel, Eugen; Chertkoff, Raul;
Almon-Brill, Einat; Zimran, Ari;
| Konferencijski rad | Mp kategorija će biti prikazana naknadno. |
2018 | Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1 (✓) | Mistry, Pramod K.; Balwani, Manisha; Baris, Hagit N.; Turkia, Hadhami Ben; Burrow, T. Andrew; Charrow, Joel; Cox, Gerald F.; Danda, Sumita; Dragosky, Marta; Drelichman, Guillermo;
El-Beshlawy, Amal; Fraga, Cristina; Freisens, Selena; Gaemers, Sebastiaan; Hadjiev, Evgueniy; Kishnani, Priya S.; Lukina, Elena; Maison-Blanche, Pierre; Martins, Ana Maria; Pastores, Gregory; Petakov, Milan ; Peterschmitt, M. Judith; Rosenbaum, Hanna; Rosenbloom, Barry; Underhill, Lisa H.; Cox, Timothy M.;
| Naučni članak | 23M23 - Rad u međ. časopisu |