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Преглед према Аутор Pastores, Gregory
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Година | Наслов | Аутор(и) | Тип резултата | Мп-кат. |
---|---|---|---|---|
2019 | Addendum to Letter to the Editor: Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1 (✓) | Mistry, Pramod K.; Balwani, Manisha; Baris, Hagit N.; Turkia, Hadhami Ben; Burrow, T. Andrew; Charrow, Joel; Cox, Gerald F.; Danda, Sumita; Dragosky, Marta; Drelichman, Guillermo;
El-Beshlawy, Amal; Fraga, Cristina; Freisens, Selena; Gaemers, Sebastiaan; Hadjiev, Evgueniy; Kishnani, Priya S.; Lukina, Elena; Maison-Blanche, Pierre; Martins, Ana Maria; Pastores, Gregory; Petakov, Milan ; Peterschmitt, M. Judith; Rosenbaum, Hanna; Rosenbloom, Barry; Underhill, Lisa H.; Cox, Timothy M.;
| Научни чланак | 22M22 - Рад у истакнутом међ. часопису |
2015 | Effect of Oral Eliglustat on Splenomegaly in Patients With Gaucher Disease Type 1 | Mistry, Pramod K.; Lukina, Elena; Ben, Turkia Hadhami; Amato, Dominick; Baris, Hagit; Dasouki, Majed; Ghosn, Marwan; Mehta, Atul; Packman, Seymour; Pastores, Gregory; | Научни чланак | 21aM21a - Рад у међ. часопису изузетних вредности |
2017 | Outcomes after 18 months of eliglustat therapy in treatment-naïve adults with Gaucher disease type 1: The phase 3 ENGAGE trial | Mistry, Pramod K.; Lukina, Elena; Ben, Turkia Hadhami; Shankar, Suma P.; Baris, Hagit; Ghosn, Marwan; Mehta, Atul; Packman, Seymour; Pastores, Gregory; Petakov, Milan ;
Assouline, Sarit; Balwani, Manisha; Danda, Sumita; Hadjiev, Evgueniy; Ortega, Andres; Gaemers, Sebastiaan J. M.; Tayag, Regina; Peterschmitt, M. Judith;
| Научни чланак | 21M21 - Рад у врхунском међ. часопису |
2018 | Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1 (✓) | Mistry, Pramod K.; Balwani, Manisha; Baris, Hagit N.; Turkia, Hadhami Ben; Burrow, T. Andrew; Charrow, Joel; Cox, Gerald F.; Danda, Sumita; Dragosky, Marta; Drelichman, Guillermo;
El-Beshlawy, Amal; Fraga, Cristina; Freisens, Selena; Gaemers, Sebastiaan; Hadjiev, Evgueniy; Kishnani, Priya S.; Lukina, Elena; Maison-Blanche, Pierre; Martins, Ana Maria; Pastores, Gregory; Petakov, Milan ; Peterschmitt, M. Judith; Rosenbaum, Hanna; Rosenbloom, Barry; Underhill, Lisa H.; Cox, Timothy M.;
| Научни чланак | 23M23 - Рад у међ. часопису |