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Преглед према Аутор Amato, Dominick J

Приказ резултата 1 до 7 од 7
ГодинаНасловАутор(и)Тип резултатаМп-кат.
2013A phase 3, randomized, double-blind, placebo-controlled, multi-center study to investigate the efficacy and safety of eliglustat in patients with Gaucher disease type 1 (ENGAGE): Results after 9 months of treatmentMistry, Pramod K; Lukina, Elena; Ben, Dridi Marie-Francoise; Amato, Dominick J; Baris, Hagit; Dasouki, Majed; Ghosn, Marwan; Mehta, Atul; Packman, Seymour; Pastores, Gregory M;
Petakov, Milan S; Peterschmitt, Judith M;
Конференцијски рад
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2012Long Term Safety and Efficacy Data of Taliglucerase Alfa, a Plant Cell Expressed Recombinant Glucocerebrosidase, in Treatment Of Naive Gaucher Disease PatientsZimran, Ari; Heitner, Rene; Mehta, Atul; Giraldo, Pllar; Rosenbaum, Hanna; Giona, Florina; Amato, Dominick J; Petakov, Milan S; Meillon, Garcia Luis Antonio; Solorio, Meza Sergio Eduardo;
Duran, Gloria; Elstein, Deborah; Brill-Almon, Einat;
Конференцијски рад
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2013Long-term safety and efficacy data of taliglucerase alfa, a Plant cell-expressed recombinant glucocerebrosidase, in the treatment of naive Gaucher disease patients: 36-Month ResultsZimran, Ari; Mehta, Atul; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Amato, Dominick J; Petakov, Milan S; Terreros, Munoz Eduardo; Eduardo, Solorio-Meza Sergio; Duran, Gloria;
Elstein, Deborah; Chertkoff, Raul; Brill-Almon, Einat;
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2012Pivotal trial with plant cell-expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher disease (Erratum - errors in Affiliations - vol 118, pg 5767, 2011)</strong></font>Zimran, Ari; Brill-Almon, Einat; Chertkoff, Raul; Petakov, Milan S; Blanco-Favela, Francisco; Munoz, Eduardo Terreros; Solorio, Meza Sergio Eduardo; Amato, Dominick J; Duran, Gloria; Giona, Florina;
Heitner, Rene; Rosenbaum, Hanna; Giraldo, Pilar; Mehta, Atul; Park, Glen; Phillips, Mici; Elstein, Deborah; Altarescu, Gheona; Szleifer, Mali; Hashmueli, Sharon; Aviezer, David;
Остало
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2011Plant Cell Expressed Recombinant Glucocerebrosidase - taliglucerase alfa - as Therapy for Gaucher Disease in Patients Previously Treated with imiglucerasePastores, Gregory M; Fernhoff, Paul M; Szer, Jeffrey; Petakov, Milan S; Cox, Timothy M; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J; Mengel, Eugen; Chertkoff, Raul;
Almon-Brill, Einat; Zimran, Ari;
Конференцијски рад
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2012Plant Cell Expressed Recombinant Glucocerebrosidase - Taliglucerase alfa as Therapy for Gaucher Disease in Patients Previously Treated with ImiglucerasePastores, Gregory M; Fernhoff, Paul M; Szer, Jeffrey; Petakov, Milan S; Cox, Timothy M; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J; Mengel, Eugen; Chertkoff, Raul;
Almon-Brill, Einat; Zimran, Ari;
Конференцијски рад
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2013Plant cell-expressed recombinant glucocerebrosidase: Taliglucerase alfa as therapy for Gaucher disease in adults patients previously treated with imiglucerase: 24-month resultsPastores, Gregory M; Shankar, Suma P; Szer, Jeffrey; Petakov, Milan S; Cox, Timothy M; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J; Mengel, Eugen; Chertkoff, Raul;
Almon-Brill, Einat; Zimran, Ari;
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