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Преглед према Аутор Peterschmitt, M. Judith

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ГодинаНасловАутор(и)Тип резултатаМп-кат.
2019Addendum to Letter to the Editor: Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1 (✓)Mistry, Pramod K.; Balwani, Manisha; Baris, Hagit N.; Turkia, Hadhami Ben; Burrow, T. Andrew; Charrow, Joel; Cox, Gerald F.; Danda, Sumita; Dragosky, Marta; Drelichman, Guillermo;
El-Beshlawy, Amal; Fraga, Cristina; Freisens, Selena; Gaemers, Sebastiaan; Hadjiev, Evgueniy; Kishnani, Priya S.; Lukina, Elena; Maison-Blanche, Pierre; Martins, Ana Maria; Pastores, Gregory; Petakov, Milan  ; Peterschmitt, M. Judith; Rosenbaum, Hanna; Rosenbloom, Barry; Underhill, Lisa H.; Cox, Timothy M.;
Научни чланак
22M22 - Рад у истакнутом међ. часопису
2015Effect of Oral Eliglustat on Splenomegaly in Patients With Gaucher Disease Type 1Mistry, Pramod K.; Lukina, Elena; Ben, Turkia Hadhami; Amato, Dominick; Baris, Hagit; Dasouki, Majed; Ghosn, Marwan; Mehta, Atul; Packman, Seymour; Pastores, Gregory;
Petakov, Milan  ; Assouline, Sarit; Balwani, Manisha; Danda, Sumita; Hadjiev, Evgueniy; Ortega, Andres; Shankar, Suma; Solano, Maria Helena; Ross, Leorah; Angell, Jennifer; Peterschmitt, M. Judith;
Научни чланак
21aM21a - Рад у међ. часопису изузетних вредности
2017Outcomes after 18 months of eliglustat therapy in treatment-naïve adults with Gaucher disease type 1: The phase 3 ENGAGE trialMistry, Pramod K.; Lukina, Elena; Ben, Turkia Hadhami; Shankar, Suma P.; Baris, Hagit; Ghosn, Marwan; Mehta, Atul; Packman, Seymour; Pastores, Gregory; Petakov, Milan  ;
Assouline, Sarit; Balwani, Manisha; Danda, Sumita; Hadjiev, Evgueniy; Ortega, Andres; Gaemers, Sebastiaan J. M.; Tayag, Regina; Peterschmitt, M. Judith;
Научни чланак
21M21 - Рад у врхунском међ. часопису
2018Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1 (✓)Mistry, Pramod K.; Balwani, Manisha; Baris, Hagit N.; Turkia, Hadhami Ben; Burrow, T. Andrew; Charrow, Joel; Cox, Gerald F.; Danda, Sumita; Dragosky, Marta; Drelichman, Guillermo;
El-Beshlawy, Amal; Fraga, Cristina; Freisens, Selena; Gaemers, Sebastiaan; Hadjiev, Evgueniy; Kishnani, Priya S.; Lukina, Elena; Maison-Blanche, Pierre; Martins, Ana Maria; Pastores, Gregory; Petakov, Milan  ; Peterschmitt, M. Judith; Rosenbaum, Hanna; Rosenbloom, Barry; Underhill, Lisa H.; Cox, Timothy M.;
Научни чланак
23M23 - Рад у међ. часопису