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Преглед према Аутор Rosenbaum, Hanna

Приказ резултата 1 до 14 од 14
ГодинаНасловАутор(и)Тип резултатаМп-кат.
2019Addendum to Letter to the Editor: Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1 (✓)Mistry, Pramod K.; Balwani, Manisha; Baris, Hagit N.; Turkia, Hadhami Ben; Burrow, T. Andrew; Charrow, Joel; Cox, Gerald F.; Danda, Sumita; Dragosky, Marta; Drelichman, Guillermo;
El-Beshlawy, Amal; Fraga, Cristina; Freisens, Selena; Gaemers, Sebastiaan; Hadjiev, Evgueniy; Kishnani, Priya S.; Lukina, Elena; Maison-Blanche, Pierre; Martins, Ana Maria; Pastores, Gregory; Petakov, Milan  ; Peterschmitt, M. Judith; Rosenbaum, Hanna; Rosenbloom, Barry; Underhill, Lisa H.; Cox, Timothy M.;
Научни чланак
22M22 - Рад у истакнутом међ. часопису
2016Enzyme replacement therapy with taliglucerase alfa: 36‐month safety and efficacy results in adult patients with Gaucher disease previously treated with imiglucerasePastores, Gregory M.; Shankar, Suma P.; Petakov, Milan  ; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J.; Szer, Jeffrey; Chertkoff, Raul; Brill‐Almon, Einat; Zimran, AriНаучни чланак
21M21 - Рад у врхунском међ. часопису
2012Long Term Bone Marrow Responses, as Measured by Quantitative Chemical Shift Imaging (QCSI) MRI, Following Treatment With Taliglucerase Alfa in Patients with Type 1 Gaucher Diseasevan, Dussen Laura; Hollak, Carla EM; Zimran, Ari; Petakov, Milan S; Rosenbaum, Hanna; Aviezer, David; Brill-Almon, Einat; Chertkoff, Raul; Maas, MarioКонференцијски рад
Мп категорија ће бити приказана накнадно.
2012Long Term Safety and Efficacy Data of Taliglucerase Alfa, a Plant Cell Expressed Recombinant Glucocerebrosidase, in Treatment Of Naive Gaucher Disease PatientsZimran, Ari; Heitner, Rene; Mehta, Atul; Giraldo, Pllar; Rosenbaum, Hanna; Giona, Florina; Amato, Dominick J; Petakov, Milan S; Meillon, Garcia Luis Antonio; Solorio, Meza Sergio Eduardo;
Duran, Gloria; Elstein, Deborah; Brill-Almon, Einat;
Конференцијски рад
Мп категорија ће бити приказана накнадно.
2016Long-term efficacy and safety results of taliglucerase alfa through 5 years in adult treatment-naive patients with Gaucher diseaseChertkoff, Raul; Zimran, Ari; Duran, Gloria; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Petakov, Milan S; Eduardo, Solorio-Meza Sergio; Cooper, Peter A; Varughese, Sheeba;
Alon, Sari; Brill-Almon, Einat;
Конференцијски рад
Мп категорија ће бити приказана накнадно.
2019Long-term efficacy and safety results of taliglucerase alfa through 5 years in adult treatment-naïve patients with Gaucher disease (✓)Zimran, Ari; Durán, Gloria; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Petakov, Milan  ; Terreros, Muñoz Eduardo; Solorio-Meza, Sergio Eduardo; Cooper, Peter A.; Varughese, Sheeba;
Alon, Sari; Chertkoff, Raul;
Научни чланак
22M22 - Рад у истакнутом међ. часопису
2013Long-term safety and efficacy data of taliglucerase alfa, a Plant cell-expressed recombinant glucocerebrosidase, in the treatment of naive Gaucher disease patients: 36-Month ResultsZimran, Ari; Mehta, Atul; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Amato, Dominick J; Petakov, Milan S; Terreros, Munoz Eduardo; Eduardo, Solorio-Meza Sergio; Duran, Gloria;
Elstein, Deborah; Chertkoff, Raul; Brill-Almon, Einat;
Конференцијски рад
Мп категорија ће бити приказана накнадно.
2016Long‐term efficacy and safety results of taliglucerase alfa up to 36 months in adult treatment‐naïve patients with Gaucher diseaseZimran, Ari; Durán, Gloria; Mehta, Atul; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Amato, Dominick J.; Petakov, Milan  ; Muñoz, Eduardo Terreros; Solorio‐Meza, Sergio Eduardo;
Cooper, Peter A.; Varughese, Sheeba; Chertkoff, Raul; Brill‐Almon, Einat;
Научни чланак
21M21 - Рад у врхунском међ. часопису
2012Pivotal trial with plant cell-expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher disease (Erratum - errors in Affiliations - vol 118, pg 5767, 2011)</strong></font>Zimran, Ari; Brill-Almon, Einat; Chertkoff, Raul; Petakov, Milan S; Blanco-Favela, Francisco; Munoz, Eduardo Terreros; Solorio, Meza Sergio Eduardo; Amato, Dominick J; Duran, Gloria; Giona, Florina;
Heitner, Rene; Rosenbaum, Hanna; Giraldo, Pilar; Mehta, Atul; Park, Glen; Phillips, Mici; Elstein, Deborah; Altarescu, Gheona; Szleifer, Mali; Hashmueli, Sharon; Aviezer, David;
Остало
Мп категорија ће бити приказана накнадно.
2011Pivotal trial with plant cell–expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher diseaseZimran, Ari; Brill-Almon, Einat; Chertkoff, Raul; Petakov, Milan  ; Blanco-Favela, Francisco; Muñoz, Eduardo Terreros; Solorio-Meza, Sergio E.; Amato, Dominick; Duran, Gloria; Giona, Fiorina;
Heitner, Rene; Rosenbaum, Hanna; Giraldo, Pilar; Mehta, Atul; Park, Glen; Phillips, Mici; Elstein, Deborah; Altarescu, Gheona; Szleifer, Mali; Hashmueli, Sharon; Aviezer, David;
Научни чланак
21aM21a - Рад у међ. часопису изузетних вредности
2011Plant Cell Expressed Recombinant Glucocerebrosidase - taliglucerase alfa - as Therapy for Gaucher Disease in Patients Previously Treated with imiglucerasePastores, Gregory M; Fernhoff, Paul M; Szer, Jeffrey; Petakov, Milan S; Cox, Timothy M; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J; Mengel, Eugen; Chertkoff, Raul;
Almon-Brill, Einat; Zimran, Ari;
Конференцијски рад
Мп категорија ће бити приказана накнадно.
2012Plant Cell Expressed Recombinant Glucocerebrosidase - Taliglucerase alfa as Therapy for Gaucher Disease in Patients Previously Treated with ImiglucerasePastores, Gregory M; Fernhoff, Paul M; Szer, Jeffrey; Petakov, Milan S; Cox, Timothy M; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J; Mengel, Eugen; Chertkoff, Raul;
Almon-Brill, Einat; Zimran, Ari;
Конференцијски рад
Мп категорија ће бити приказана накнадно.
2013Plant cell-expressed recombinant glucocerebrosidase: Taliglucerase alfa as therapy for Gaucher disease in adults patients previously treated with imiglucerase: 24-month resultsPastores, Gregory M; Shankar, Suma P; Szer, Jeffrey; Petakov, Milan S; Cox, Timothy M; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J; Mengel, Eugen; Chertkoff, Raul;
Almon-Brill, Einat; Zimran, Ari;
Конференцијски рад
Мп категорија ће бити приказана накнадно.
2018Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1 (✓)Mistry, Pramod K.; Balwani, Manisha; Baris, Hagit N.; Turkia, Hadhami Ben; Burrow, T. Andrew; Charrow, Joel; Cox, Gerald F.; Danda, Sumita; Dragosky, Marta; Drelichman, Guillermo;
El-Beshlawy, Amal; Fraga, Cristina; Freisens, Selena; Gaemers, Sebastiaan; Hadjiev, Evgueniy; Kishnani, Priya S.; Lukina, Elena; Maison-Blanche, Pierre; Martins, Ana Maria; Pastores, Gregory; Petakov, Milan  ; Peterschmitt, M. Judith; Rosenbaum, Hanna; Rosenbloom, Barry; Underhill, Lisa H.; Cox, Timothy M.;
Научни чланак
23M23 - Рад у међ. часопису