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Browsing by Author Taruscio, Domenica

Showing results 1 to 2 of 2
Issue DateTitleAuthor(s)TypeМp-cat.
2020A call for global action for rare diseases in AfricaBaynam, Gareth S.; Groft, Stephen; van der Westhuizen, Francois H.; Gassman, Safiyya D.; du Plessis, Kelly; Coles, Emily P.; Selebatso, Eda; Selebatso, Moses; Gaobinelwe, Boikobo; Selebatso, Tebogo;
Joel, Dipesalema; Llera, Virginia A.; Vorster, Barend C.; Wuebbels, Barbara; Djoudalbaye, Benjamin; Austin, Christopher P.; Kumuthini, Judit; Forman, John; Kaufmann, Petra; Chipeta, James; Gavhed, Desiree; Larsson, Annika; Stojiljković, Maja  ; Nordgren, Ann; Roldan, Emilio J. A.; Taruscio, Domenica; Wong-Rieger, Durhane; Nowak, Kristen; Bilkey, Gemma A.; Easteal, Simon; Bowdin, Sarah; Reichardt, Juergen K. V.; Beltran, Sergi; Kosaki, Kenjiro; van Karnebeek, Clara D. M.; Gong, Mengchun; Zhang, Shuyang; Mehrian-Shai, Ruty; Adams, David R.; Puri, Ratna D.; Zhang, Feng; Pachter, Nicholas; Muenke, Maximilian; Nellaker, Christoffer; Gahl, William A.; Cederroth, Helene; Broley, Stephanie; Schoonen, Maryke; Boycott, Kym M.; Posada, Manuel;
Article
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2013The TREAT-NMD Duchenne Muscular Dystrophy Registries: Conception, Design, and Utilization by Industry and AcademiaBladen, Catherine L.; Rafferty, Karen; Straub, Volker; Monges, Soledad; Moresco, Angélica; Dawkins, Hugh; Roy, Anna; Chamova, Teodora; Guergueltcheva, Velina; Korngut, Lawrence;
Campbell, Craig; Dai, Yi; Barišić, Nina; Kos, Tea; Brabec, Petr; Rahbek, Jes; Lahdetie, Jaana; Tuffery-Giraud, Sylvie; Claustres, Mireille; Leturcq, France; Ben, Yaou Rabah; Walter, Maggie C.; Schreiber, Olivia; Karcagi, Veronika; Herczegfalvi, Agnes; Viswanathan, Venkatarman; Bayat, Farhad; de, la caridad Guerrero Sarmiento Isis; Ambrosini, Anna; Ceradini, Francesca; Kimura, En; van, den Bergen Janneke C.; Rodrigues, Miriam; Roxburgh, Richard; Lusakowska, Anna; Oliveira, Jorge; Santos, Rosário; Neagu, Elena; Butoianu, Niculina; Artemieva, Svetlana; Rasic, Vedrana Milic; Posada, Manuel; Palau, Francesc; Lindvall, Björn; Bloetzer, Clemens; Karaduman, Ayşe; Topaloğlu, Haluk; Inal, Serap; Oflazer, Piraye; Stringer, Angela; Shatillo, Andriy V.; Martin, Ann S.; Peay, Holly; Flanigan, Kevin M.; Salgado, David; von, Rekowski Brigitta; Lynn, Stephen; Heslop, Emma; Gainotti, Sabina; Taruscio, Domenica; Kirschner, Jan; Verschuuren, Jan; Bushby, Kate; Béroud, Christophe; Lochmüller, Hanns;
Article
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