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Long-Term Evaluation of Givinostat in Duchenne Muscular Dystrophy, and Natural History Comparisons [2025]
McDonald, Craig M; ...; Vucinic, Dragana; ...; (broj, koautora 25)Altered PLP1 splicing causes hypomyelination of early myelinating structures [2015]
Kevelam, Sietske H.; Taube, Jennifer R.; van, Spaendonk Rosalina M. L.; Bertini, Enrico; Sperle, Karen; Tarnopolsky, Mark; Tonduti, Davide; Valente, Enza Maria; Travaglini, Lorena; Sistermans, Erik A.;
Bernard, Geneviève; Catsman-Berrevoets, Coriene E.; van, Karnebeek Clara D. M.; Østergaard, John R.; Friederich, Richard L.; Fawzi, Elsaid Mahmoud; Schieving, Jolanda H.; Tarailo Graovac, Maja 
; Orcesi, Simona; Steenweg, Marjan E.; van, Berkel Carola G. M.; Waisfisz, Quinten; Abbink, Truus E. M.; van, der Knaap Marjo S.; Hobson, Grace M.; Wolf, Nicole I.;
; Orcesi, Simona; Steenweg, Marjan E.; van, Berkel Carola G. M.; Waisfisz, Quinten; Abbink, Truus E. M.; van, der Knaap Marjo S.; Hobson, Grace M.; Wolf, Nicole I.; Filters
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