Pretraga

Rezultati

A Phase 3, multicenter, open-label, switchover trial to assess the safety and efficacy of taliglucerase alfa, a plant cell-expressed recombinant human glucocerebrosidase, in adult and pediatric patients with Gaucher disease previously treated with imiglucerase [2014]

Pastores, Gregory; Petakov, Milan ; Giraldo, P.; Rosenbaum, H.; Szer, J.; Deegan, PB; Amato, DJ; Mengel, E.; Tan, ES; Chertkoff, R.;

Brill-Almon, E.; Zimran, A.;

Compound heterozygosity for the Cretan type of non-deletional hereditary persistence of fetal hemoglobin and beta-thalassemia or Hb Sabine confirms the functional role of the A gamma-158 C gt T mutation in gamma-globin gene transcription [2008]

Kollia, Panagoula; Kalamaras, Angelos; Chassanidis, Christos; Samara, Maria; Vamvakopoulos, Nikolaos K.; Ugrin, Milena ; Pavlović, Sonja ; Papadakis, Manoussos N.; Patrinos, George P.

Significant and continuous improvement in bone mineral density among type 1 Gaucher disease patients treated with velaglucerase alfa: 69-month experience, including dose reduction [2011]

Elstein, Deborah; Foldes, A. Joseph; Zahrieh, David; Cohn, Gabriel M.; Djordjevic, Maja; Brutaru, Costin; Zimran, Ari

Acquired von Willebrand syndrome in patients with Gaucher disease [2014]

Mitrović, Mirjana ; Elezović, Ivo ; Miljić, Predrag ; Suvajdžić-Vuković, Nada

Addendum to Letter to the Editor: Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1 [2019]

Mistry, Pramod K.; Balwani, Manisha; Baris, Hagit N.; Turkia, Hadhami Ben; Burrow, T. Andrew; Charrow, Joel; Cox, Gerald F.; Danda, Sumita; Dragosky, Marta; Drelichman, Guillermo;

El-Beshlawy, Amal; Fraga, Cristina; Freisens, Selena; Gaemers, Sebastiaan; Hadjiev, Evgueniy; Kishnani, Priya S.; Lukina, Elena; Maison-Blanche, Pierre; Martins, Ana Maria; Pastores, Gregory; Petakov, Milan ; Peterschmitt, M. Judith; Rosenbaum, Hanna; Rosenbloom, Barry; Underhill, Lisa H.; Cox, Timothy M.;

Appendiceal involvement in a patient with Gaucher disease [2018]

Kocić, Marija; Đuričić, Slaviša M.; Đorđević, Maja ; Savić, Đorđe ; Kecman, Božica; Sarajlija, Adrijan

Long-term efficacy and safety results of taliglucerase alfa through 5 years in adult treatment-naïve patients with Gaucher disease [2019]

Zimran, Ari; Durán, Gloria; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Petakov, Milan ; Terreros, Muñoz Eduardo; Solorio-Meza, Sergio Eduardo; Cooper, Peter A.; Varughese, Sheeba;

Alon, Sari; Chertkoff, Raul;

Long-term safety and efficacy of taliglucerase alfa in pediatric Gaucher disease patients who were treatment-naïve or previously treated with imiglucerase [2018]

Zimran, Ari; Gonzalez-Rodriguez, Derlis Emilio; Abrahamov, Aya; Cooper, Peter A.; Varughese, Sheeba; Giraldo, Pilar; Petakov, Milan ; Tan, Ee Shien; Chertkoff, Raul

Early achievement and maintenance of the therapeutic goals using velaglucerase alfa in type 1 Gaucher disease [2011]

Elstein, D.; Cohn, G.M.; Wang, N.; Djordjevic, M.; Brutaru, C.; Zimran, A.

Gene expression profiling in fetal and adult definitive erythropoiesis [2007]

Čokić, Vladan ; Bhattacharya, Bhaskar; Smith, Reginald D.; Beleslin-Čokić, Bojana ; Noguchi, Constance T.; Puri, Raj K.; Schechter, Alan N.