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Research outputs
A Phase 3, multicenter, open-label, switchover trial to assess the safety and efficacy of taliglucerase alfa, a plant cell-expressed recombinant human glucocerebrosidase, in adult and pediatric patients with Gaucher disease previously treated with imiglucerase
[2014]
Pastores, Gregory; Petakov, Milan
Brill-Almon, E.; Zimran, A.;
Appendiceal involvement in a patient with Gaucher disease
[2018]
Kocić, Marija; Đuričić, Slaviša M.; Đorđević, Maja Addendum to Letter to the Editor: Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1
[2019]
Mistry, Pramod K.; Balwani, Manisha; Baris, Hagit N.; Turkia, Hadhami Ben; Burrow, T. Andrew; Charrow, Joel; Cox, Gerald F.; Danda, Sumita; Dragosky, Marta; Drelichman, Guillermo;
El-Beshlawy, Amal; Fraga, Cristina; Freisens, Selena; Gaemers, Sebastiaan; Hadjiev, Evgueniy; Kishnani, Priya S.; Lukina, Elena; Maison-Blanche, Pierre; Martins, Ana Maria; Pastores, Gregory; Petakov, Milan
; Peterschmitt, M. Judith; Rosenbaum, Hanna; Rosenbloom, Barry; Underhill, Lisa H.; Cox, Timothy M.;
Acquired von Willebrand syndrome in patients with Gaucher disease
[2014]
Mitrović, Mirjana Significant and continuous improvement in bone mineral density among type 1 Gaucher disease patients treated with velaglucerase alfa: 69-month experience, including dose reduction [2011]
Elstein, Deborah; Foldes, A. Joseph; Zahrieh, David; Cohn, Gabriel M.; Djordjevic, Maja; Brutaru, Costin; Zimran, AriCompound heterozygosity for the Cretan type of non-deletional hereditary persistence of fetal hemoglobin and beta-thalassemia or Hb Sabine confirms the functional role of the A gamma-158 C gt T mutation in gamma-globin gene transcription [2008]
Kollia, Panagoula; Kalamaras, Angelos; Chassanidis, Christos; Samara, Maria; Vamvakopoulos, Nikolaos K.; Ugrin, MilenaEarly achievement and maintenance of the therapeutic goals using velaglucerase alfa in type 1 Gaucher disease [2011]
Elstein, D.; Cohn, G.M.; Wang, N.; Djordjevic, M.; Brutaru, C.; Zimran, A.Long-term safety and efficacy of taliglucerase alfa in pediatric Gaucher disease patients who were treatment-naïve or previously treated with imiglucerase
[2018]
Zimran, Ari; Gonzalez-Rodriguez, Derlis Emilio; Abrahamov, Aya; Cooper, Peter A.; Varughese, Sheeba; Giraldo, Pilar; Petakov, Milan Gammopathy and B lymphocyte clonality in patients with Gaucher type I disease
[2013]
Rodić, Predrag Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1
[2018]
Mistry, Pramod K.; Balwani, Manisha; Baris, Hagit N.; Turkia, Hadhami Ben; Burrow, T. Andrew; Charrow, Joel; Cox, Gerald F.; Danda, Sumita; Dragosky, Marta; Drelichman, Guillermo;
El-Beshlawy, Amal; Fraga, Cristina; Freisens, Selena; Gaemers, Sebastiaan; Hadjiev, Evgueniy; Kishnani, Priya S.; Lukina, Elena; Maison-Blanche, Pierre; Martins, Ana Maria; Pastores, Gregory; Petakov, Milan
; Peterschmitt, M. Judith; Rosenbaum, Hanna; Rosenbloom, Barry; Underhill, Lisa H.; Cox, Timothy M.;
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