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Clinical Trial Readiness for Spinal Muscular Atrophy: Experience of an International Educational-Training Initiative
| Title: | Clinical Trial Readiness for Spinal Muscular Atrophy: Experience of an International Educational-Training Initiative | Authors: | Tizzano, Eduardo F; Christie-Brown, Vanessa; Baranello, Giovanni; Germanenko, Olga; Gray, Allyson; Krstic, Marija; Lilien, Charlotte; Patel, Hinal; Servais, Laurent; Scoto, Mariacristina | Issue Date: | 2022 | Publication: | JOURNAL OF NEUROMUSCULAR DISEASES | ISSN: | 2214-3599 Journal of Neuromuscular Diseases Search Idenfier |
Type: | Article | Collation: | vol. 9 br. 6 str. 809-820 | DOI: | 10.3233/JND-221538 | WoS-ID: | 000886925100011 | Scopus-ID: | 2-s2.0-85141933872 | URI: | https://enauka.gov.rs/handle/123456789/802751 | Project: | Cure SMA Industry Consortium (IC) in the US AveXis, Inc Biogen Genentech/Roche Pharmaceuticals Novartis Astellas Pharmaceuticals Cytokinetics Inc Ionis Pharmaceuticals, Inc. Scholar Rock |
Metadata source: | (Preuzeto iz Nasi u WoS) | M-category: | 21M21 |
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