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eNauka >  Rezultati >  Clinical Trial Readiness for Spinal Muscular Atrophy: Experience of an International Educational-Training Initiative
Naziv: Clinical Trial Readiness for Spinal Muscular Atrophy: Experience of an International Educational-Training Initiative
Autori: Tizzano, Eduardo F; Christie-Brown, Vanessa; Baranello, Giovanni; Germanenko, Olga; Gray, Allyson; Krstic, Marija; Lilien, Charlotte; Patel, Hinal; Servais, Laurent; Scoto, Mariacristina
Godina: 2022
Publikacija: JOURNAL OF NEUROMUSCULAR DISEASES
ISSN: 2214-3599 Journal of Neuromuscular Diseases Pretraži identifikator
Tip rezultata: Naučni članak
Kolacija: vol. 9 br. 6 str. 809-820
DOI: 10.3233/JND-221538
WoS-ID: 000886925100011
Scopus-ID: 2-s2.0-85141933872
URI: https://enauka.gov.rs/handle/123456789/802751
Projekat: Cure SMA Industry Consortium (IC) in the US
AveXis, Inc
Biogen
Genentech/Roche Pharmaceuticals
Novartis
Astellas Pharmaceuticals
Cytokinetics Inc
Ionis Pharmaceuticals, Inc.
Scholar Rock
Izvor metapodataka: (Preuzeto iz Nasi u WoS)
M-kategorija: 
21M21 - Vodeći međunarodni časopis kategorije M21

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